Scientists Discover Drug That Reverses Rare Blood Disorder by Boosting Protein Production
Researchers found that inhibiting LSD1 enzyme increases SEC23A protein levels, potentially treating congenital anemia.
2294 articles in this topic
Researchers found that inhibiting LSD1 enzyme increases SEC23A protein levels, potentially treating congenital anemia.
Engineered zinc finger therapy reduced pain-sensing gene activity by 50% in primates for 6 months without major side effects.
New research reveals pancreatic beta cells actively contribute to autoimmune attack in type 1 diabetes through faulty stress responses.
Breakthrough prodrug technology enables oral delivery of allopregnanolone, showing promise for treating anxiety and mood disorders.
New MRI technique measures heart oxygen efficiency in 3 minutes, potentially revolutionizing early heart disease detection.
Revolutionary delivery system uses red blood cells to program immune cells in the spleen to fight cancer tumors.
Scientists map 2.56 million cells from pregnant pig and fetus, discovering how heart adapts during pregnancy and what causes growth restriction.
Breakthrough imaging reveals how telomerase protects chromosome ends, offering new insights into cellular aging mechanisms.
Scientists discover how specific DNA features allow cells to remember past inflammation, potentially impacting aging and disease.
Experimental BIIB094 treatment lowered harmful LRRK2 protein levels in spinal fluid, offering hope for genetic Parkinson's patients.
Researchers developed PANGEA-SMM, which tracks changing biomarkers to predict when precancerous blood conditions become active cancer.
Breakthrough treatment targets cancers with p53 mutations, offering hope for previously difficult-to-treat tumors.